Gene editing is a highly precise and powerful technology that allows scientists to insert, delete, modify or replace DNA ...

A lot of effort has gone into finding ways to minimize or eliminate off-target edits. In a recent issue of Nature, ...

An infant named KJ Muldoon, born with a severe and typically fatal genetic disorder called CPS1 deficiency, is now walking and talking after receiving a one-of-a-kind, patient-specific gene-editing ...

Scientists have made many advances using traditional CRISPR technology, especially in medicine, but they are now seeking ways ...

A handful of start-up firms are testing therapies that target specific epigenetic markers to treat everything from high cholesterol to a rare muscular disorder ...

A six year old in China passed away after she underwent an experimental gene-editing treatment for a rare neurodevelopmental ...

A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based gene editing to treat a child with a rare genetic disorder. Unlike earlier ...

A 6-year-old Chinese girl died last year after receiving an experimental gene therapy to correct a non-life-threatening ...

CRISPR Therapeutics offers a diversified gene-editing pipeline, with CASGEVY as its lead asset and multiple upcoming ...

The reported death of a six-year-old Chinese girl days after receiving an experimental brain-targeted gene-editing therapy ...

Megan covers the intersection of science and society. How is biomedical research funded? Who benefits? And how do new technologies reflect and shape our values? You can reach Megan on Signal at ...

It has also aggressively invested in gene editing, including its 2025 acquisition of cardiovascular disease gene-editing ...